Servizio dei Vettori

Pubblicazioni Scientifiche

• 2012 PLOS ONE

  Nivalenol and Deoxynivalenol Affect Rat Intestinal Epithelial Cells: A Concentration Related Study

• 2013 HUM GENE THER METHOD

  AAV2/8 Vectors Purified from Culture Medium with a Simple and Rapid Protocol Transduce Murine Liver, Muscle, and Retina Efficiently

• 2014 PROGRESS IN RETINAL AND EYE RESEARCH

  Vector platforms for gene therapy of inherited retinopathies

• 2012 EMBO MOLECULAR MEDICINE

  Effective AAV-mediated gene therapy in a mouse model of ethylmalonic encephalopathy

• 2013 PLOS ONE

  Myosin7a Deficiency Results in Reduced Retinal Activity Which Is Improved by Gene Therapy

• 2015 HUMAN GENE THERAPY CLINICAL DEVELOPMENT

  A Clinical Trial of Gene Therapy for Mucopolysaccharidosis VI, a Severe Lysosomal Storage Disorder (MeuSIX)

• 2012 CIRCULATION RESEARCH

  Viral Gene Transfer Rescues Arrhythmogenic Phenotype and Ultrastructural Abnormalities in Adult Calsequestrin-Null Mice With Inherited Arrhythmias

• 2014 GENE THERAPY

  Retinal transduction profiles by high-capacity viral vectors